Report Detail

Pharmaceuticals & Healthcare Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Pipeline Review, H2 2019

  • RnM3868733
  • |
  • 16 January, 2020
  • |
  • Global
  • |
  • 39 Pages
  • |
  • Global Markets Direct
  • |
  • Pharmaceuticals & Healthcare

Table of Contents

    List of Tables

      List of Figures


          Global Markets Direct Report Coverage

            Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Overview

              Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Therapeutics Development

                Pipeline Overview

                  Pipeline by Companies

                    Pipeline by Universities/Institutes

                      Products under Development by Companies

                        Products under Development by Universities/Institutes

                          Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Therapeutics Assessment

                            Assessment by Target

                              Assessment by Mechanism of Action

                                Assessment by Route of Administration

                                  Assessment by Molecule Type

                                    Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Companies Involved in Therapeutics Development

                                      Axovant Gene Therapies Ltd

                                        IntraBio Ltd

                                          Orphi Therapeutics Inc

                                            Polaryx Therapeutics Inc

                                              Recursion Pharmaceuticals Inc

                                                Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Drug Profiles

                                                  Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Dormant Projects

                                                    Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Discontinued Products

                                                      Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Product Development Milestones


                                                        Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Pipeline Review, H2 2019


                                                        Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Pipeline Review, H2 2019, provides an overview of the Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) pipeline landscape.

                                                        Sandhoff disease is an inherited lipid storage disorder that progressively destroys nerve cells (neurons) in the brain and spinal cord. It is caused by a deficiency of the enzyme beta-hexosaminidase. Symptoms include progressive nervous system deterioration, problems initiating and controlling muscles and movement, increased startle reaction to sound, early blindness, seizures, spasticity, and myoclonus. Treatment includes anticonvulsants to control seizures.

                                                        Report Highlights

                                                        Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Pipeline Review, H2 2019, provides comprehensive information on the therapeutics under development for Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

                                                        The Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Sandhoff Disease (Jatzkewitz-Pilz Syndrome) and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase II, Preclinical and Discovery stages are 2, 4 and 1 respectively. Similarly, the Universities portfolio in Phase I stages comprises 1 molecules, respectively.

                                                        Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

                                                        Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.


                                                        - The pipeline guide provides a snapshot of the global therapeutic landscape of Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders).
                                                        - The pipeline guide reviews pipeline therapeutics for Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
                                                        - The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
                                                        - The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
                                                        - The pipeline guide reviews key companies involved in Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) therapeutics and enlists all their major and minor projects.
                                                        - The pipeline guide evaluates Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
                                                        - The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
                                                        - The pipeline guide reviews latest news related to pipeline therapeutics for Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders)

                                                        Reasons to buy

                                                        - Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
                                                        - Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
                                                        - Find and recognize significant and varied types of therapeutics under development for Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders).
                                                        - Classify potential new clients or partners in the target demographic.
                                                        - Develop tactical initiatives by understanding the focus areas of leading companies.
                                                        - Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
                                                        - Formulate corrective measures for pipeline projects by understanding Sandhoff Disease (Jatzkewitz-Pilz Syndrome) (Genetic Disorders) pipeline depth and focus of Indication therapeutics.
                                                        - Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
                                                        - Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

                                                        Get latest Market Research Reports on Sandhoff Disease (Jatzkewitz-Pilz Syndrome). Industry analysis & Market Report on Sandhoff Disease (Jatzkewitz-Pilz Syndrome) is a syndicated market report, published as Sandhoff Disease (Jatzkewitz-Pilz Syndrome) - Pipeline Review, H2 2019. It is complete Research Study and Industry Analysis of Sandhoff Disease (Jatzkewitz-Pilz Syndrome) market, to understand, Market Demand, Growth, trends analysis and Factor Influencing market.

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